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Disease Reportsleber congenital amaurosis
MeSH D057130 - leber congenital amaurosis
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Competitive Landscape
Events Timeline
Commercial
Clinical Trials
Competitive landscape
D015785:Hereditary eye diseases
0 Companies
0 Drugs
Success rate
D012164:Retinal diseases
$
Success rate
D057130: 
Leber congenital amaurosis
$
Success rate
Events Timeline
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Commercial
Company Name
Drug Name
Trade Name
Patent Expires
Approval Date
Revenue
Period
NovartisVoretigene neparvovec Luxturna  2018-11-22   
Clinical Trials
Historical Success Rate
Phase 1
90%
9/10
Phase 2
22%
2/9
Phase 3
67%
2/3
Approved: 1Overall Success rate: 13%
All Clinical Trials
No data
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